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Accurate Quantification of AAV Vector Genomes by Quantitative PCR.

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Martinez-Fernandez de la Camara C. et al, (2021), Genes (Basel), 12

AAV Induced Expression of Human Rod and Cone Opsin in Bipolar Cells of a Mouse Model of Retinal Degeneration

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McClements ME. et al, (2021), BioMed Research International, 2021

An analysis of the Kozak consensus in retinal genes and its relevance to gene therapy.

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McClements ME. et al, (2021), Mol Vis, 27, 233 - 242

CRISPR genome engineering for retinal diseases.

Chapter

Kantor A. et al, (2021), 182, 29 - 79

Is subretinal AAV gene replacement still the only viable treatment option for choroideremia?

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Han RC. et al, (2021), Expert Opin Orphan Drugs, 9, 13 - 24

Genome editing strategies for treating human retinal degenerations.

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Quinn J. et al, (2020), Hum Gene Ther

Association of a Novel Intronic Variant in RPGR With Hypomorphic Phenotype of X-Linked Retinitis Pigmentosa.

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Cehajic-Kapetanovic J. et al, (2020), JAMA Ophthalmol

CRISPR-Cas9 DNA Base-Editing and Prime-Editing.

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Kantor A. et al, (2020), Int J Mol Sci, 21

CRISPR Interference-Potential Application in Retinal Disease.

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Peddle CF. et al, (2020), Int J Mol Sci, 21

Enhancement of Adeno-Associated Virus-Mediated Gene Therapy Using Hydroxychloroquine in Murine and Human Tissues.

Journal article

Chandler LC. et al, (2019), Mol Ther Methods Clin Dev, 14, 77 - 89

Molecular Strategies for RPGR Gene Therapy.

Journal article

Cehajic Kapetanovic J. et al, (2019), Genes (Basel), 10

AAV2/8 Anti-angiogenic Gene Therapy Using Single-Chain Antibodies Inhibits Murine Choroidal Neovascularization.

Journal article

Hughes CP. et al, (2019), Mol Ther Methods Clin Dev, 13, 86 - 98

Clinical and Molecular Characterization of PROM1-Related Retinal Degeneration.

Journal article

Cehajic-Kapetanovic J. et al, (2019), JAMA Netw Open, 2

The Location of Exon 4 Mutations in RP1 Raises Challenges for Genetic Counseling and Gene Therapy.

Journal article

Nanda A. et al, (2019), Am J Ophthalmol, 202, 23 - 29

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