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Minicircle Delivery to the Neural Retina as a Gene Therapy Approach.

Journal article

Staurenghi F. et al, (2022), Int J Mol Sci, 23

New CRISPR Tools to Correct Pathogenic Mutations in Usher Syndrome.

Journal article

Major L. et al, (2022), Int J Mol Sci, 23

Tropism of AAV Vectors in Photoreceptor-Like Cells of Human iPSC-Derived Retinal Organoids.

Journal article

McClements ME. et al, (2022), Transl Vis Sci Technol, 11

CRISPR Systems Suitable for Single AAV Vector Delivery.

Journal article

Stevanovic M. et al, (2021), Curr Gene Ther

Characterizing the cellular immune response to subretinal AAV gene therapy in the murine retina.

Journal article

Chandler LC. et al, (2021), Mol Ther Methods Clin Dev, 22, 52 - 65

Accurate Quantification of AAV Vector Genomes by Quantitative PCR.

Journal article

Martinez-Fernandez de la Camara C. et al, (2021), Genes (Basel), 12

Genome-Editing Strategies for Treating Human Retinal Degenerations.

Journal article

Quinn J. et al, (2021), Hum Gene Ther, 32, 247 - 259

AAV Induced Expression of Human Rod and Cone Opsin in Bipolar Cells of a Mouse Model of Retinal Degeneration

Journal article

McClements ME. et al, (2021), BioMed Research International, 2021

An analysis of the Kozak consensus in retinal genes and its relevance to gene therapy.

Journal article

McClements ME. et al, (2021), Mol Vis, 27, 233 - 242

CRISPR genome engineering for retinal diseases.

Chapter

Kantor A. et al, (2021), 182, 29 - 79

Is subretinal AAV gene replacement still the only viable treatment option for choroideremia?

Journal article

Han RC. et al, (2021), Expert Opin Orphan Drugs, 9, 13 - 24

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