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Publications

Beneficial effects on vision in patients undergoing retinal gene therapy for choroideremia.

Xue K. et al, (2018), Nat Med, 24, 1507 - 1512

Stroma-derived IL-6, G-CSF and Activin-A mediated dedifferentiation of lung carcinoma cells into cancer stem cells.

Rodrigues CFD. et al, (2018), Sci Rep, 8

Choroideremia: molecular mechanisms and development of AAV gene therapy.

Patrício MI. et al, (2018), Expert Opin Biol Ther, 18, 807 - 820

The Biological Activity of AAV Vectors for Choroideremia Gene Therapy Can Be Measured by In Vitro Prenylation of RAB6A.

Patrício MI. et al, (2018), Mol Ther Methods Clin Dev, 9, 288 - 295

Retinal Degeneration in Choroideremia follows an Exponential Decay Function.

Aylward JW. et al, (2018), Ophthalmology

A clinical-grade gene therapy vector for pharmacoresistant epilepsy successfully overexpresses NPY in a human neuronal cell line.

Patrício MI. et al, (2018), Seizure, 55, 25 - 29

Human Retinal Explant Culture for Ex Vivo Validation of AAV Gene Therapy.

Orlans HO. et al, (2018), 1715, 289 - 303

Novel non-contiguous exon duplication in choroideremia.

Edwards TL. et al, (2018), Clin Genet, 93, 144 - 148

Retinal Gene Therapy for Choroideremia: In Vitro Testing for Gene Augmentation Using an Adeno-Associated Viral (AAV) Vector.

Patrício MI. and MacLaren RE., (2018), 1715, 89 - 97

Impact of Vital Dyes on Cell Viability and Transduction Efficiency of AAV Vectors Used in Retinal Gene Therapy Surgery: An In Vitro and In Vivo Analysis.

Salvetti AP. et al, (2017), Transl Vis Sci Technol, 6

Prenylation of Rab6a as a Potency Assay for Choroideremia Gene Therapy

Patricio MI. et al, (2017), MOLECULAR THERAPY, 25, 142 - 143

Inclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human Retina.

Patrício MI. et al, (2017), Mol Ther Nucleic Acids, 6, 198 - 208

Acetylated bacterial cellulose coated with urinary bladder matrix as a substrate for retinal pigment epithelium.

Gonçalves S. et al, (2016), Colloids Surf B Biointerfaces, 139, 1 - 9

Rab11b mediates melanin transfer between donor melanocytes and acceptor keratinocytes via coupled exo/endocytosis.

Tarafder AK. et al, (2014), J Invest Dermatol, 134, 1056 - 1066

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