Targeting GLB1 in mice by CRISPR/Cas9 genome editing: Establishing a novel model for type II GM1 gangliosidosis

Nicoli E-R., Han T., Yoon R., Glase B., Latour Y., Huebecker M., D'Souza A., Peiravi M., Tyrlik M., Springer D., Jeeva JM., Donahue D., Sidhu R., Kell P., Jiang X., Acosta M., Platt FM., Proia RL., Tifft CJ.

DOI

10.1016/j.ymgme.2019.11.300

Type

Conference paper

Publication Date

02/2020

Volume

129

Pages

S116 - S116

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