Publisher Correction: Therapies for rare diseases: therapeutic modalities, progress and challenges ahead.
Tambuyzer E., Vandendriessche B., Austin CP., Brooks PJ., Larsson K., Needleman KIM., Valentine J., Davies K., Groft SC., Preti R., Oprea TI., Prunotto M.
An amendment to this paper has been published and can be accessed via a link at the top of the paper.